Lumacaftor-ivacaftor (Orkambi) for cystic fibrosis: behind the 'breakthrough'.
Mayer M.
Evid Based Med · journal article · DOI 10.1136/ebmed-2015-110325 PUBLICATION REGISTRY
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Publikationer som ChEBI hänvisar till för Orkambi. Visa hela publikationsregistret
A publication hit is not a conclusion. Publikationslistan visar bibliografiska uppgifter. Eventuella forskningsutdrag visas separat med originalunderlag. En källhänvisning visar inte i sig effekt, dosering eller säkerhet.
Publications in the selection
7 hitsLumacaftor alone and combined with ivacaftor: preclinical and clinical trial experience of F508del CFTR correction.
Brewington JJ, McPhail GL, Clancy JP.
Expert Rev Respir Med · research support, non-u.s. gov't; journal article · DOI 10.1586/17476348.2016.1122527Response to: 'Lumacaftor/ivacaftor for patients homozygous for Phe508del-CFTR: should we curb our enthusiasm?' by Jones and Barry.
Elborn JS, Ramsey B, Wainwright C, Boyle M.
Thorax · letter; comment · DOI 10.1136/thoraxjnl-2015-207611Lumacaftor-Ivacaftor in Patients with Cystic Fibrosis Homozygous for Phe508del CFTR.
Rehman A, Baloch NU, Janahi IA.
N Engl J Med · letter; comment · DOI 10.1056/nejmc1510466Lumacaftor and ivacaftor in the management of patients with cystic fibrosis: current evidence and future prospects.
Kuk K, Taylor-Cousar JL.
Ther Adv Respir Dis · research support, non-u.s. gov't; review; journal article; research support, n.i.h., extramural · DOI 10.1177/1753465815601934Lumacaftor/ivacaftor for patients homozygous for Phe508del-CFTR: should we curb our enthusiasm?
Jones AM, Barry PJ.
Thorax · editorial · DOI 10.1136/thoraxjnl-2015-207369Lumacaftor-Ivacaftor in Patients with Cystic Fibrosis Homozygous for Phe508del CFTR.
Wainwright CE, Elborn JS, Ramsey BW, Marigowda G, Huang X, Cipolli M, Colombo C, Davies JC, De Boeck K, Flume PA, Konstan MW, McColley SA, McCoy K, McKone EF, Munck A, Ratjen F, Rowe SM, Waltz D, Boyle MP, TRAFFIC Study Group, TRANSPORT Study Group.
N Engl J Med · clinical trial, phase iii; research support, non-u.s. gov't; research-article; multicenter study; randomized controlled trial; journal article; research support, n.i.h., extramural · DOI 10.1056/nejmoa1409547